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▲Upstaza简介（图片来源：参考资料[2]）

参考资料：

[1] PTC Therapeutics Receives Positive CHMP Opinion for Upstaza™ for the Treatment of AADC Deficiency. Retrieved May 20, 2022, from https://www.prnewswire.com/news-releases/ptc-therapeutics-receives-positive-chmp-opinion-for-upstaza-for-the-treatment-of-aadc-deficiency-301551996.html

[2] Tai et al., (2021). Long-term efficacy and safety of eladocagene exuparvovec in patients with AADC deficiency. Molecular Therapy, https://doi.org/10.1016/j.ymthe.2021.11.005

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